Global Liver Institute
Pediatric & Rare Liver News
GLOBAL LIVER INSTITUTE
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New this month: Copayment assistance for certain genetic/metabolic diseases and a second-line PBC therapy! – Pediatric & Rare Liver Diseases News
We are honored to have had the opportunity to represent the rare liver diseases community at the Alpha-1 Foundation National Conference in Miami, Florida. The weekend was filled with transformative research and thought-provoking conversations.
Biomarker identified for infants with alpha-1 antitrypsin deficiency – Pediatric & Rare Liver Diseases News
The GLI Pediatric and Rare Liver Diseases team was thrilled to attend the BARE Symposium on May 10-11, 2024.
A Spotlight on Rare Maternal Health – Pediatric & Rare Liver Diseases News
In April, GLI Program Director Kristin Hatcher was invited to engage with patient advocacy groups, industry partners, and patients during the PBC Foundation’s International Summit in Edinburgh, Scotland.
Celebrating the benefits of drug repurposing for pediatric rare liver disease patients – Pediatric & Rare Liver Diseases News
Global Liver Institute (GLI) celebrates a major breakthrough with the U.S. FDA’s approval for Mirum Pharmaceuticals’s Livmarli (maralixibat chloride) to address cholestatic pruritus in patients aged 5 and above with progressive familial intrahepatic cholestasis (PFIC).
Rare Advocacy on Capitol Hill, in the White House, & Beyond! – Pediatric & Rare Liver Diseases News
In February, GLI raised awareness and amplified the patient voice in discussions about transitions in care for rare liver diseases. Here are a few highlights.
It’s Rare Liver Diseases Month! – Pediatric & Rare Liver Diseases News
It’s Rare Liver Diseases Month!
If you haven’t already, join us for the 2024 #RareAware multifaceted campaign, focusing on the theme of “Transitions in Care During.”